Clinical Trials for Phenylketonuria (PKU)
There are 20 clinical trials for Phenylketonuria (PKU), with 20 actively recruiting participants. Phase breakdown: Not Applicable: 8, : 6, Phase 1 / Phase 2: 2. Always talk to your doctor about whether a clinical trial is right for you.
Key Data
| Metric | Value |
|---|---|
| Total Trials | 20 |
| Recruiting Now | 20 |
| Not Applicable | 8 |
| 6 | |
| Phase 1 / Phase 2 | 2 |
| Phase 3 | 2 |
| Early Phase 1 | 1 |
| Phase 2 | 1 |
| Active Sponsors | 10 |
Top Sponsors
- BioMarin Pharmaceutical (3 trials)
- Otsuka Pharmaceutical Development & Commercialization, Inc. (2 trials)
- University of Missouri-Columbia (2 trials)
- Emory University (2 trials)
- University Children's Hospital, Zurich (1 trials)
Data sourced from ClinicalTrials.gov. Last updated 2026-04-06. This site does not provide medical advice.