Clinical Trials for Sanfilippo Syndrome
There are 2 clinical trials for Sanfilippo Syndrome, with 2 actively recruiting participants. Phase breakdown: Phase 2 / Phase 3: 2. Always talk to your doctor about whether a clinical trial is right for you.
Key Data
| Metric | Value |
|---|---|
| Total Trials | 2 |
| Recruiting Now | 2 |
| Phase 2 / Phase 3 | 2 |
| Active Sponsors | 2 |
Top Sponsors
- Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center (1 trials)
- Ultragenyx Pharmaceutical Inc (1 trials)
Data sourced from ClinicalTrials.gov. Last updated 2026-04-06. This site does not provide medical advice.