Clinical Trials for Mucopolysaccharidosis II
There are 3 clinical trials for Mucopolysaccharidosis II, with 3 actively recruiting participants. Phase breakdown: Phase 2 / Phase 3: 1, Phase 1: 1, : 1. Always talk to your doctor about whether a clinical trial is right for you.
Key Data
| Metric | Value |
|---|---|
| Total Trials | 3 |
| Recruiting Now | 3 |
| Phase 2 / Phase 3 | 1 |
| Phase 1 | 1 |
| 1 | |
| Active Sponsors | 3 |
Top Sponsors
- Denali Therapeutics Inc. (1 trials)
- Joanne Kurtzberg, MD (1 trials)
- University of California, San Francisco (1 trials)
Data sourced from ClinicalTrials.gov. Last updated 2026-04-06. This site does not provide medical advice.