Clinical Trials for Pompe Disease
There are 22 clinical trials for Pompe Disease, with 22 actively recruiting participants. Phase breakdown: : 11, Not Applicable: 4, Phase 4: 2. Always talk to your doctor about whether a clinical trial is right for you.
Key Data
| Metric | Value |
|---|---|
| Total Trials | 22 |
| Recruiting Now | 22 |
| 11 | |
| Not Applicable | 4 |
| Phase 4 | 2 |
| Phase 1 / Phase 2 | 2 |
| Phase 3 | 1 |
| Phase 1 | 1 |
| Phase 2 | 1 |
| Active Sponsors | 10 |
Top Sponsors
- Genzyme, a Sanofi Company (3 trials)
- Duke University (2 trials)
- Amicus Therapeutics (2 trials)
- University of California, San Francisco (2 trials)
- xCures (1 trials)
Data sourced from ClinicalTrials.gov. Last updated 2026-04-06. This site does not provide medical advice.