RECRUITINGOBSERVATIONAL
ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)
ConTTRibute: A Global Observational Multicenter Long-Term Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)
About This Trial
The purpose of this study is to: * Describe epidemiological and clinical characteristics, natural history and real-world clinical management of ATTR amyloidosis patients * Characterize the safety and effectiveness of patisiran and vutrisiran as part of routine clinical practice in the real-world clinical setting * Describe disease emergence/progression in pre-symptomatic carriers of a known disease-causing transthyretin (TTR) variant
Who May Be Eligible (Plain English)
Who May Qualify:
- Diagnosis of ATTR amyloidosis or documented known disease-causing TTR variant for the cohort of pre-symptomatic carriers
- Germany Only: Patients must be treated per the summary of product characteristics (SmPC) for any approved treatment for ATTR amyloidosis
Who Should NOT Join This Trial:
- Current enrollment in a clinical trial for any investigational agent
Always talk to your doctor about whether this trial is right for you.
Original Eligibility Criteria
View original clinical language
Inclusion Criteria:
* Diagnosis of ATTR amyloidosis or documented known disease-causing TTR variant for the cohort of pre-symptomatic carriers
* Germany Only: Patients must be treated per the summary of product characteristics (SmPC) for any approved treatment for ATTR amyloidosis
Exclusion Criteria:
* Current enrollment in a clinical trial for any investigational agent
Locations (20)
Clinical Trial Site
La Jolla, California, United States
Clinical Trial Site
Los Angeles, California, United States
Clinical Trial Site
Jacksonville, Florida, United States
Clinical Trial Site
Iowa City, Iowa, United States
Clinical Trial Site
Kansas City, Kansas, United States
Clinical Trial Site
Baltimore, Maryland, United States
Clinical Trial Site
Boston, Massachusetts, United States
Clinical Trial Site
New York, New York, United States
Clinical Trial Site
Durham, North Carolina, United States
Clinical Trial Site
Columbus, Ohio, United States
Clinical Trial Site
Philadelphia, Pennsylvania, United States
Clinical Trial Site
Austin, Texas, United States
Clinical Trial Site
Houston, Texas, United States
Clinical Trial Site
Salvador, Brazil
Clinical Trial Site
São Paulo, Brazil
Clinical Trial Site
Sofia, Bulgaria
Clinical Trial Site
Aarhus, Denmark
Clinical Trial Site
Copenhagen, Denmark
Clinical Trial Site
Bordeaux, France
Clinical Trial Site
Bron, France